a genetic disorder where the body doesn't produce enough AAT protein. The interim readout is expected in the second half of ...

The Series B funds will support the launch of a Phase I/II clinical trial for AIR-001 to advance its RNA editing pipeline.

An interesting application of AAT is in the treatment of people with eating disorders such as anorexia nervosa and bulimia nervosa. This innovative therapeutic method includes animals, most ...

AATD is an inherited genetic disorder that can cause early onset of ... dose-dependent increases in total and functional alpha-1 antitrypsin (AAT). Also, new production of corrected protein ...

AATD is an inherited genetic disorder that can cause early onset emphysema ... correction of the disease-causing mutation and total AAT protein levels above the therapeutic threshold in the ...