News

This cumulative increase in linear growth corresponds to an increase in the height z score (referenced to achondroplasia-specific growth charts) of 0.54 (95% CI, 0.35 to 0.72) at month 18 .
This increase in growth translated into an increase in z-score of +0.29 standard deviation scores compared to achondroplasia growth charts. Treatment has been well tolerated, ...
The study involved 72 children with achondroplasia from Australia, the UK, the US, Spain, France and Canada. It reported the medication was effective at increasing the rate of growth by 2.5 cm a ...
BridgeBio’s drug, a pill called infigratinib, increased the pace of growth by about 3 centimeters per year from baseline for a cohort of 10 children with achondroplasia, a rare genetic disorder ...
COPENHAGEN, Denmark, May 13, 2025 (GLOBE NEWSWIRE) -- Ascendis Pharma A/S (Nasdaq: ASND) today announced new data showing improvements in growth and bone morphometry from Week 52 of its pivotal ...
A promising daily tablet is effective at increasing height and improving proportional limb growth in children with achondroplasia, the most common form of dwarfism, according to a new study.
RIBOMIC Announces Positive Interim Results from Phase IIa Trial of umedaptanib pegol in Achondroplasia Demonstrating Increase in Annualized Growth Rate of up to +4.6 cm/year in Children 5 Years ...
Achondroplasia is a rare genetic condition arising from a systemic fibroblast growth factor receptor 3 (FGFR3) variant that leads to an imbalance in the effects of the FGFR3 and CNP signaling ...
Achondroplasia is a rare genetic condition arising from a systemic fibroblast growth factor receptor 3 (FGFR3) variant that leads to an imbalance in the effects of the FGFR3 and CNP signaling ...