In a study published in Science Advances, University of Alabama at Birmingham researchers led by Kasey Brida and Jeremy Day, ...

Clustered, regularly interspaced short palindromic repeats (CRISPR) and CRISPR-associated protein 9 (CRISPR-Cas9) are genome ...

Beam Therapeutics BEAM announced that the FDA has granted an orphan drug designation to its investigational genome-editing ...

Shares lost a quarter of their value after the company disclosed, in a regulatory filing, signs of liver stress in a study ...

Scientists have used personalised gene-editing therapy to successfully treat a baby with a rare genetic condition. Could this ...

Gene therapy experts and advocates warning of the sector’s many challenges found a receptive audience in FDA leadership at a ...

This research roundup discusses researchers’ attempts to find a treatment for a “brain fog” that comes with CAR T-Cell ...

A baby born with a rare and dangerous genetic disease is growing and thriving after getting an experimental gene editing ...