Repositioning genes awakens fetal hemoglobin to treat disease. CRISPR editing may change future gene therapy. Researchers ...

Gene therapy is the insertion of genes into an individual's cells and tissues to treat a disease, and hereditary diseases in which a defective mutant allele is replaced with a functional one.

Modern medicine constantly searches for safer and more efficient ways to treat genetic disorders. One cutting-edge solution that has emerged is the use of non-viral vectors.

You can reach Katie on Signal at palmer.01. NEW YORK — To gene therapy pioneer Jim Wilson, the field is currently clouded with “irrational pessimism.” Companies are abandoning ship ...

Cell boundaries, labeled in magenta, are more organized after gene therapy, and the level of cBIN1 protein (green) is higher. Image credit: Hong Lab. “Even though the animals are still facing stress ...

Boys Treated With Gene Therapy for Rare Brain Disease Doing Well 6 Years Later By Ernie Mundell HealthDay Reporter THURSDAY, Oct.10, 2024 (HealthDay News) -- Most boys treated with breakthrough ...

One gene therapy trial in OA is under way and another in RA is close to reaching human study, but that’s a year or more away. The road for gene therapies in RA is complicated, costly and fraught ...