The company licensed its core technology, dubbed TransJoin, from Nationwide Children’s Hospital in Columbus, Ohio, a leading hub for gene therapy research. Nationwide’s Timothy Cripe, a ...

Baby KJ Muldoon, 1st to be treated with personalized gene therapy, released from hospital 00:45. Prior treatement, KJ was dealing with ammonia building up in his system.

Gene therapy is the insertion of genes into an individual's cells and tissues to treat a disease, and hereditary diseases in which a defective mutant allele is replaced with a functional one.

Gene therapy for blood stem cells has historically been challenging, expensive, and intrusive. Traditionally, it involved harvesting stem cells from a patient or donor, ...

Gene therapy is a revolutionary field in modern medicine, offering transformative potential to treat and potentially cure a wide range of genetic and acquired diseases. By addressing the root ...

I n a groundbreaking medical achievement, an infant from Pennsylvania, referred to as KJ, has become the first person to successfully receive a personalized CRISPR gene editing therapy.The ...

GREEN BAY, Wis. (WBAY) - A Green Bay resident has become the first Wisconsinite to receive a gene therapy treatment for hemophilia A since it was approved by the FDA in June.

A pivotal medical milestone has been reached. For the first time ever, researchers have used a personalized CRISPR-based gene therapy to treat an infant’s rare and life-threatening illness.

One gene therapy trial in OA is under way and another in RA is close to reaching human study, but that’s a year or more away. The road for gene therapies in RA is complicated, costly and fraught ...