If administered early, gene therapy has the potential to change the medical history of children born with metachromatic ...

When even one tiny section of a person’s genetic code becomes mutated or modified, cells can begin to act out of ...

Hathway’s technology uses natural epigenetic processes to dial gene activity up or down, rather than rewriting the genetic ...

"Moreover, the duration of follow-up is among the longest reported for a lentiviral vector-based gene therapy; 13 patients ...

Additionally, improving CAR-T biological efficiency could reduce dosing needs, further cutting costs and expanding access.

A major trial of a promising gene therapy for Duchenne muscular dystrophy has fallen short, but researchers say the lessons learned could pave the way for better, more effective treatments.

Lexeo Therapeutics, Inc.’s LXEO share price has surged by 9.50%, which has investors questioning if this is right time to ...

a clinical-stage gene therapy company focused on using the life-changing power of genetic medicine to reverse or prevent blindness, today announced that the U.S. Food and Drug Administration (FDA ...

A program cochair said the agenda was designed to get attendees "out of their comfort zone." The Amercian Association for ...

Sixty years ago cystic fibrosis was practically a death sentence, but the remarkable progress of science and medicine means that people with the condition can live into their 60s. What new health ...

The FDA granted regenerative medicine advanced therapy designation to ATSN-201, a gene therapy candidate for the treatment of ...

Feb. 7, 2025 — A research team has made a major discovery on how the CUL5 gene affects CAR-T cell therapy, an advanced cancer therapy. The study reveals that reducing the activity of the CUL5 ...