News

Muscular Dystrophy News4d
A day of reflection leads me to a place of gratitude as a DMD mom
After taking a day for reflection on her sons' lives with DMD, columnist Betty Vertin says she feels more on top of their care.
Business Wire3mon
Scholar Rock to Present Additional Clinical Data from the Phase 3 SAPPHIRE Trial at the 2025 Muscular Dystrophy Association (MDA) Clinical & Scientific Conference
That poster will be presented by Adam I ... patients with spinal muscular atrophy being featured at the upcoming Muscular Dystrophy Association Clinical and Scientific Conference, along with ...
The American Journal of Managed Care2mon
Real-World Study Suggests DMD Gene Therapy Is Safe, Effective
Poster P65. Veerapandiyan A, Bourke J, Day J, et al. Assessment of cardiac outcomes in delandistrogene moxeparvovec clinical trials for Duchenne muscular dystrophy. Presented at: 2025 MDA Clinical ...
Yahoo Finance28d
SonoThera™ to Present New Data at ASGCT 2025 Demonstrating the Potential of Genetic Medicine Using Targeted, Ultrasound-Mediated Delivery in Treating Duchenne Muscular ...
An oral presentation will focus on the treatment of Hemophilia A while new data in the poster session targets the treatment of Duchenne Muscular Dystrophy (DMD). Both presentations at ASGCT ...
Morningstar2mon
Avidity Biosciences Announces Upcoming Presentations at the Muscular Dystrophy Association (MDA) Clinical & Scientific Conference
will present topline del-zota data from Avidity's Phase 1/2 EXPLORE44 trial for people living with Duchenne Muscular Dystrophy amenable to exon 44 skipping (DMD44). March 16-18, 2025: 6:00 p.m ...
Yahoo Finance3mon
Scholar Rock to Present Additional Clinical Data from the Phase 3 SAPPHIRE Trial at the 2025 Muscular Dystrophy Association (MDA) Clinical & Scientific Conference
Poster presentations include preclinical data on a combination treatment approach for building muscle mass and strength in a Duchenne muscular dystrophy (DMD) model In addition, Scholar Rock will ...