In two new papers, researchers from The Jackson Laboratory (JAX) report the successful use of two approaches -- gene therapy ...
Arcturus Therapeutics Holdings Inc. (NASDAQ:ARCT), a commercial-stage biotechnology company with a market capitalization of ...
In two new papers, researchers from The Jackson Laboratory (JAX) report the successful use of two approaches—gene therapy and ...
To report SUSPECTED ADVERSE REACTIONS, contact Zevra Therapeutics, Inc. at toll-free phone 1-844-600-2237 or FDA at 1‐800-FDA-1088 or .
“Ten years ago, it was our hope that by focusing on comprehensively characterizing a single, albeit rare, disease we could ...
SEED Therapeutics announced that the U.S. Food and Drug Administration has granted Rare Pediatric Disease and Orphan Drug designations to ...
FLC is a rare liver cancer with unique genetic traits, often misdiagnosed until advanced. New research and a clinical trial ...
Discover the importance of vision, genetic eye disorders, and RNA-based therapies for precision treatment in India and ...
India should eliminate tax on drugs for cancer treatment and for chronic and rare diseases, the chairperson of major ...
This case study explores a rare overlap of hidradenitis suppurativa and porokeratosis, as well as highlights the unique ...
AB2 Bio signs U.S. option and licensing agreement with Nippon Shinyaku for Tadekinig alfa for an ultra-rare autoimmune disease AB2 Bio Ltd Sun, Jan 26, 2025, 11:30 PM 5 min read ...