The death of a patient in a trial of an experimental gene therapy casts new shadows over a technology once seen as the future ...

While the medical world is melting down from the absolute apocalypse that is RFK Jr., it's good to celebrate that (at least ...

Cell and gene therapy (C&GT) is set to revolutionise treatment of complex diseases, offering new possibilities for patients.

For 21-year-old Javarian Weatherspoon, life without pain feels like a miracle. After growing up with sickle cell disease, he ...

In medical breakthrough, a baby diagnosed with rare genetic disorder is thriving after customized CRISPR gene editing therapy ...

KJ Muldoon came into the world with a genetic time bomb ticking inside him.

Sickle cell disease doesn’t discriminate, but it does disproportionately affect those with the least access to healthcare ...

Alfred E. Mann Charities has made a generous gift of $12 million to establish the Alfred E. Mann Cell and Gene Therapy ...

A personalized gene editing therapy was successfully used to treat an infant with CPS1 deficiency, a disease that causes ...

With a better upfront offer on the table, enough bluebird bio investors have tendered their shares for the company's sale to ...