Health on MSN12mon
What Is Beta Thalassemia?
With beta thalassemia, your body lacks sufficient amounts of healthy red blood cells with hemoglobin, and anemia develops, ...
MedPage Today4h
Gene Therapy May Be a Game Changer for Transfusion-Dependent Thalassemia
The FDA approved betibeglogene autotemcel (beti-cel; Zynteglo) for adult and pediatric patients with transfusion-dependent ...
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MCH levels in blood test: What do they mean?
Hemoglobinopathies like beta thalassemia The symptoms of low MCH include: High MCH is seen in people with macrocytic anemia or large red blood cells. These are associated with deficiency of ...
Nature1y
Genetic Mutation
Molecules of sickle-cell hemoglobin stick to one another, forming rigid rods. These rods cause a person's red blood cells to take on a deformed, sickle-like ... One form of beta-thalassemia ...
2minutemedicine.com2d
Beti-cel gene therapy achieves high rates of transfusion independence in severe β-thalassemia
There were no serious adverse events or treatment-related mortalities. Evidence Rating Level: 2 (Good) Study Rundown: Transfusion-dependent β-thalassemia (TDT) is a condition that results in iron ...
pharmaphorum2y
Commercialization of novel gene-editing technology in beta-thalassemia
Beta-thalassemia is a rare blood disorder caused by a genetic defect ... and it raises concerns for my future and what my life expectancy will look like. The disease has triggered other health ...