To improve outcomes, neonates with significant comorbidities such as sepsis and perinatal asphyxia on a background of FNAIT should be closely monitored. The prevalence of fetal and neonatal alloimmune ...

Clinicians changed their treatment plan in 19.4% of the paired pre- and post-MSDA time points, after reviewing the MSDA results. The multiple sclerosis (MS) disease activity (MSDA) blood test shows ...

ATTR-PN is an incurable disorder in which the achieving of meaningful improvement remains an important clinical goal. Hereditary transthyretin amyloidosis can result in significant morbidity; in ...

Patients who were treated with inebilizumab had a greater reduction in the Myasthenia Gravis Activities of Daily Living scale and the Quantitative Myasthenia Gravis scale scores at week 26 compared to ...

Astragaloside II (AS-II) exerted its activity by suppressing β-catenin/inhibitors of DNA binding 2 (Id2)/myelin basic protein (MBP) signaling. Astragaloside II (AS-II) improves neurobehavioral ...

Michael Lingzhi Li, PhD, assistant professor in the technology and operations management unit at Harvard Business School, Boston, Massachusetts, speaks at WODC 2025 (Photo by Riya Ajmera) Speakers ...

(L-R) Rare Disease Advisor senior correspondent Larry Luxner, patient columnists Alithea Athans, Tara Keith and Tom Bartlett, and director of advocacy relations Vera Luxner (Photo by Riya Ajmera) ...

Paclitaxel protein-bound, but not doxorubicin liposome injection, reduced the number of cells expressing Fc epsilon receptor I, the immunoglobulin E receptor. Researchers have developed and validated ...

The study will measure annualized bleeding rate, joint bleeds, spontaneous bleeds, activated partial thromboplastin time, and inhibitor development. A new study is set to evaluate the effectiveness of ...

The tool addressed gaps in exposure to rare bleeding disorders often missing in traditional curricula. An online, case-based learning tool significantly enhanced trainee confidence and perceived ...

Speakers at the panel “Unlocking the future: the convergence of AI, personalized medicine, and genomics” at the World Orphan Drug Congress USA 2025 (Photo by Riya Ajmera) Artificial intelligence could ...

There is a correlation between the expression levels of Thy-1 in the portal areas and the extent of liver fibrosis. The expression levels of thymocyte differentiation antigen 1 (Thy-1) are associated ...