A child born with a life-threatening genetic disorder has been successfully treated using pioneering ethical gene therapy.

Find more information on the Altmetric Attention Score and how the score is calculated. Single molecule enzymology provides an opportunity to examine details of enzyme mechanisms that are not ...

The personalized CRISPR treatment could be the future of gene therapy, but hurdles remain before everyone has access.

Find more information on the Altmetric Attention Score and how the score is calculated. We show that diffusion of single urease enzyme molecules increases in the presence of urea in a ...

Genetic defects are exceedingly common, which is not surprising considering just how many cells make up our bodies, including our reproductive cells. While most of these defects have no or only ...

In 2012, scientists Jennifer Doudna and Emmanuelle Charpentier replicated this mechanism found in microbes to develop a ...

In medical breakthrough, a baby diagnosed with rare genetic disorder is thriving after customized CRISPR gene editing therapy ...

Scientists working at the NIH’s BRAIN Initiative have created new viral vectors that one day could lead to gene therapies for ...

In a stunning medical breakthrough that effectively brings designer babies out of the realm of science fiction, a ...

The child will need to be monitored throughout his life, but researchers said the treatment’s success indicates that other ...

While the medical world is melting down from the absolute apocalypse that is RFK Jr., it's good to celebrate that (at least ...