Becker muscular dystrophy (BMD) is a type of muscular dystrophy, a genetic condition that weakens and damages muscles. It can worsen with age. However, its symptoms are less severe than those of ...
The mum of an 11-year-old boy who is waiting to find out if he can access a new drug to treat his Duchenne muscular dystrophy (DMD) said her son talked about his fear of death. Harry, from Corby ...
A patient has died following treatment with Elevidys, the Sarepta Therapeutics product that is the only FDA-approved gene therapy for Duchenne muscular dystrophy, the company disclosed Tuesday.
its FDA-approved treatment for Duchenne muscular dystrophy. In a statement, the Cambridge, Massachusetts-based biotech said that a young man with DMD died after receiving Elevidys, a gene therapy ...
Considering taking supplements to treat muscular dystrophy? Below is a list of common natural remedies used to treat or reduce the symptoms of muscular dystrophy. Follow the links to read common ...
A young person with Duchenne muscular dystrophy died following treatment with the recently approved gene therapy ...
A close friend of 30 years recently asked what my life was like before I was diagnosed with limb-girdle muscular dystrophy. We then talked about what I’d already known when I was diagnosed in 1985, as ...
(AP Photo/Manuel Balce Ceneta, File) Updated [hour]:[minute] [AMPM] [timezone], [monthFull] [day], [year] WASHINGTON (AP) — Sarepta Therapeutics said Tuesday that a patient died while taking its ...
A young man with Duchenne muscular dystrophy (DMD) who received the one-time gene therapy Elevidys (delandistrogene moxeparvovec-rokl) has died due to acute liver failure. In a statement, the ...
Spinal muscular atrophy (SMA) is a disorder affecting the motor neurons—nerve cells that control voluntary muscle movement. These cells are located in the spinal cord. Because the muscles cannot ...