C&EN7d
12 drug candidates debut in San Diego
BMS-986458 features three stereocenters, one of which epimerizes easily, Mortensen said. The drug candidate, which would be ...
Yale Environment 36016d
New CRISPR tool enables more seamless gene editing — and improved disease modeling
Advances in the gene-editing technology known as CRISPR-Cas9 over the past 15 years have yielded important new insights into the roles that specific genes play in many diseases. But to date this ...
University of California16d
Breathing new life: Working toward an inhalable gene therapy for cystic fibrosis
The disease is caused by mutations in one gene — cystic fibrosis transmembrane conductance regulator, or CFTR — making it, in theory, an ideal candidate for gene-editing technology. However, there’s a ...
NME16d
Gene on reuniting for first live show in over 20 years: “We don’t want any half measures – it needs to be spectacular”
The original Gene line-up have reunited and announced their first live show in over 20 years. Read NME‘s interview with frontman Martin Rossiter below, where he discusses what to expect from the ...
Muscular Dystrophy News17d
Sarepta reports death of DMD patient given gene therapy Elevidys
A young man with Duchenne muscular dystrophy (DMD) who received the one-time gene therapy Elevidys (delandistrogene moxeparvovec-rokl) has died due to acute liver failure. In a statement, the ...
Alzheimer's Research UK19d
Genes and dementia
These pages give an overview of what genes are and how they are involved in the different diseases that cause dementia. You will also find information about genetic testing for dementia. Genes ...
The Independent19d
Alzheimer’s and a rare disease: Everything we know about Gene Hackman and wife’s deaths
From reproductive rights to climate change to Big Tech, The Independent is on the ground when the story is developing. Whether it's investigating the financials of Elon Musk's pro-Trump PAC or ...
Hollywood Life21d
Gene Hackman’s Children: Meet the Late Oscar Winner’s 3 Kids
Gene Hackman had only been spotted on a few rare appearances throughout the remainder of his life. The Royal Tenenbaums star hung up his hat on his iconic film career at the age of 74, and he died ...
Healthline22d
Is ADHD Genetic?
Other research indicates a link between specific gene mutations and ADHD. Researchers found eight variants associated with ADHD. Research in this area is ongoing. More studies are needed to better ...
Forbes23d
What Gene Hackman’s Death Teaches Us About Caring For A Loved One With Dementia
Forbes contributors publish independent expert analyses and insights. Dana Feldman is a Los Angeles-based reporter who covers entertainment.
kffhealthnews25d
Scientists Correct Disease-Causing DNA Mutation Using Targeted Gene Therapy
The New York Times: Mutated DNA Restored To Normal In Gene Therapy Advance Researchers have corrected a disease-causing gene mutation with a single infusion carrying a treatment that precisely ...