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A baby born with a rare and dangerous genetic disease is growing and thriving after getting an experimental gene editing ...
After spending over 300 days at CHOP, KJ Muldoon has been released from the hospital after receiving personalized CRISPR gene ...
After spending over 300 days at CHOP, KJ Muldoon has been released from the hospital after receiving personalized CRISPR gene ...
CRISPR-based gene editing therapy has been used for the first time to treat CPS1 deficiency, which promises a new era for ...
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