Capricor Therapeutics is expected to release data from the phase 3 HOPE-3 trial in Q3'25, thus presenting a potential path ...

The Buckinghamshire man went to see his local GP. Ryan went from blood tests to muscle biopsies to DNA tests, trying to get ...

Panelists discuss how recent advancements in muscular dystrophy treatment have evolved toward truly disease-modifying therapies using gene replacement, antisense oligonucleotides, and gene ...

Duchenne muscular dystrophy – diagnosis, clinical development and global research Its impact on patients, available treatments and why early diagnosis is essential Muscular dystrophy refers to a group ...

Neurodevelopmental disorders and psychiatric symptoms in patients with dystrophinopathy may be part of a neurodevelopmental disorder associated with dystrophinopathy, although some psychiatric ...

WebMD explains the symptoms of different types of muscular dystrophy, including Duchene, Becker, and myotonic.

Symptoms of Duchenne Muscular Dystrophy DMD symptoms usually start by age 6. Symptoms may begin as early as infancy, but most boys don't have any symptoms in the first few years of their life.

Dr Anup Rawool Facioscapulohumeral muscular dystrophy (FSHD) is a genetic condition that affects muscle function, often making everyday tasks — like smiling or lifting one’s arms — difficult. For ...

Becker muscular dystrophy is like Duchenne, except milder. It also affects boys but the symptoms start later -- between ages 11 and 25. Myotonic muscular dystrophy is the most common form in adults.

Oculopharyngeal muscular dystrophy is a genetic condition that causes muscle weakness. Learn about its symptoms, causes, treatments, and more.

The degree to which novel value elements such as insurance value impact estimated treatment value for rare, severe genetic diseases such as Duchenne muscular dystrophy is unclear.